First UK child to receive Libmeldy

Posted on: 14/02/2023

The BBC have made an excellent documentary following Teddi Shaw, the first UK patient to receive transformative gene therapy for MLD, 'Libmeldy'. This is the therapy which we, and many dedicated others, fought so hard to get approved in the UK. Hats off to all involved, especially the remarkable teams at Manchester Children's Hospital and Ospedale San Raffaele in Milan and the extraordinarily strong MLD families who feature. Now we just need Newborn Screening for MLD so that all affected children can benefit before its too late. You can watch the doucmentary here:  BBC iPlayer 'Bittersweet Medicine'