Day +359 - Image 1

Day +359

Posted on: 22/03/2015

Today we flew back to Milan for Ava's  12 month post-transplant checks. We are a little ahead of the exact date, but it is tricky for the doctors to juggle monitoring all of the children on the trial, bearing in mind that Ava is number 12 out of 19; and the fact there are also around 150 children on an MLD natural history study who are regularly monitored to help research. Dr Biffi and her team have incredibly treat 7 more children with Gene Therapy in the last year, which is fantastic. They have one more child to recruit and then they will seek to register the treatment. Hopefully it will be quickly approved and can then be carried out in hospitals around the globe. In the meantime, Ava has a very demanding week of testing ahead of her, but I know she will tackle it with her usual determination and upbeat spirit. We are looking forward to catching up with the wonderful team here and praying for positive results. 



©2024 Copyright ArchAngel MLD Trust
Website by Modern Websites